
ACE-031
ACE-031 (ActRIIB-Fc Ligand Trap) is a recombinant fusion protein consisting of the extracellular domain of activin receptor type IIB (ActRIIB) linked to an IgG1…
Half-life
Approximately 10–15 days (human PK, single-dose SC)
Delivery
Subcutaneous injection; historical clinical protocols dosed every 2–4 weeks.
Suggested dosage
Not specified
Usage
Mechanism of action
Benefits (3)
- Increases lean body mass and muscle volume in human and animal studies
- May improve functional measures (e.g., 6-minute walk trends in DMD studies)
- Associated increases in bone mineral density in some models
Side effects (3)
- Epistaxis (nosebleeds) and telangiectasias reported in clinical studies
- Injection-site reactions (pain, pruritus, hematoma)
- Potential vascular effects linked to broader ligand binding (e.g., BMP9/10 cross-reactivity in class)